文献
J-GLOBAL ID:201402219364460558
整理番号:14A0507312
Rett症候群治療のためのメカセルミン(組換ヒトIGF-1)の安全性,薬物動態及び予備的有効性評価
Safety, pharmacokinetics, and preliminary assessment of efficacy of mecasermin (recombinant human IGF-1) for the treatment of Rett syndrome
著者 (30件):
KHWAJA Omar S.
(Harvard Medical School, MA)
,
KHWAJA Omar S.
(F. Hoffmann-La Roche AG, Basel, CHE)
,
HO Eugenia
(Harvard Medical School, MA)
,
HO Eugenia
(Univ. Southern California, CA)
,
BARNES Katherine V.
(Harvard Medical School, MA)
,
O’LEARY Heather M.
(Harvard Medical School, MA)
,
PEREIRA Luis M.
(Harvard Medical School, MA)
,
FINKELSTEIN Yaron
(Univ. Toronto, ON, CAN)
,
FINKELSTEIN Yaron
(Boston Children’s Hospital, MA)
,
NELSON Charles A., III
(Harvard Medical School, MA)
,
VOGEL-FARLEY Vanessa
(Harvard Medical School, MA)
,
DEGREGORIO Geneva
(Harvard Medical School, MA)
,
HOLM Ingrid A.
(Harvard Medical School, MA)
,
HOLM Ingrid A.
(Boston Children’s Hospital, MA)
,
KHATWA Umakanth
(Harvard Medical School, MA)
,
KAPUR Kush
(Harvard Medical School, MA)
,
KAPUR Kush
(Boston Children’s Hospital, MA)
,
ALEXANDER Mark E.
(Harvard Medical School, MA)
,
ALEXANDER Mark E.
(Boston Children’s Hospital, MA)
,
FINNEGAN Deirdre M.
(Harvard Medical School, MA)
,
CANTWELL Nicole G.
(Harvard Medical School, MA)
,
WALCO Alexandra C.
(Harvard Medical School, MA)
,
RAPPAPORT Leonard
(Harvard Medical School, MA)
,
GREGAS Matt
(Harvard Medical School, MA)
,
GREGAS Matt
(Boston Children’s Hospital, MA)
,
FICHOROVA Raina N.
(Harvard Medical School, MA)
,
SHANNON Michael W.
(Boston Children’s Hospital, MA)
,
SHANNON Michael W.
(Harvard Medical School, MA)
,
SUR Mriganka
(Massachusetts Inst. Technol., MA)
,
KAUFMANN Walter E.
(Harvard Medical School, MA)
資料名:
Proceedings of the National Academy of Sciences of the United States of America
(Proceedings of the National Academy of Sciences of the United States of America)
巻:
111
号:
12
ページ:
4596-4601
発行年:
2014年03月25日
JST資料番号:
D0387A
ISSN:
0027-8424
資料種別:
逐次刊行物 (A)
記事区分:
短報
発行国:
アメリカ合衆国 (USA)
言語:
英語 (EN)