文献
J-GLOBAL ID:201102225710106969
整理番号:11A0706822
ベクター投与MTopen1.5年を経たレーバーの先天性黒内障の安全性及び有効性
Gene Therapy for Leber’s Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration MTopen
著者 (31件):
SIMONELLI Francesca
(Second Univ. Naples, Naples, ITA)
,
SIMONELLI Francesca
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
MAGUIRE Albert M
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
MAGUIRE Albert M
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
TESTA Francesco
(Second Univ. Naples, Naples, ITA)
,
PIERCE Eric A
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
MINGOZZI Federico
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
BENNICELLI Jeannette L
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
ROSSI Settimio
(Second Univ. Naples, Naples, ITA)
,
MARSHALL Kathleen
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
BANFI Sandro
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
SURACE Enrico M
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
SUN Junwei
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
REDMOND T Michael
(NIH, Maryland, USA)
,
ZHU Xiaosong
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
SHINDLER Kenneth S
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
YING Gui-Shuang
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
ZIVIELLO Carmela
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
ZIVIELLO Carmela
(Inst. Genetics and Biophysics “A. Buzzati-Traverso”, CNR, Naples, ITA)
,
ACERRA Carmela
(Second Univ. Naples, Naples, ITA)
,
ACERRA Carmela
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
ACERRA Carmela
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
WRIGHT J Fraser
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
WRIGHT J Fraser
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
MCDONNELL Jennifer Wellman
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
HIGH Katherine A
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
HIGH Katherine A
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
BENNETT Jean
(Univ. Pennsylvania School of Medicine, Pennsylvania, USA)
,
BENNETT Jean
(Children’s Hospital of Philadelphia, Pennsylvania, USA)
,
AURICCHIO Alberto
(Telethon Inst. Genetics and Medicine (TIGEM), Naples, ITA)
,
AURICCHIO Alberto
(Univ. Naples “Federico II”, Naples, ITA)
資料名:
Molecular Therapy
(Molecular Therapy)
巻:
18
号:
3
ページ:
643-650
発行年:
2010年03月
JST資料番号:
W1762A
ISSN:
1525-0016
資料種別:
逐次刊行物 (A)
発行国:
オランダ (NLD)
言語:
英語 (EN)