文献
J-GLOBAL ID:201902220677075150
整理番号:19A1644279
ポリロタキサンのナノキャリアは,DMD遺伝子を成功させるために,ジストロフィー筋細胞にCRISPR/Cas9プラスミドを提供することができる【JST・京大機械翻訳】
Polyrotaxane Nanocarriers Can Deliver CRISPR/Cas9 Plasmid to Dystrophic Muscle Cells to Successfully Edit the DMD Gene
著者 (19件):
Emami Michael R.
(Molecular Biology Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Emami Michael R.
(Center for Duchenne Muscular Dystrophy, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Emami Michael R.
(Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Young Courtney S.
(Center for Duchenne Muscular Dystrophy, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Young Courtney S.
(Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Young Courtney S.
(Department of Neurology, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Ji Ying
(Division of Nanomedicine, Department of Medicine, California NanoSystems Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Liu Xiangsheng
(Division of Nanomedicine, Department of Medicine, California NanoSystems Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Mokhonova Ekaterina
(Center for Duchenne Muscular Dystrophy, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Mokhonova Ekaterina
(Department of Neurology, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Pyle April D.
(Molecular Biology Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Pyle April D.
(Center for Duchenne Muscular Dystrophy, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Pyle April D.
(Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Pyle April D.
(Department of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Meng Huan
(Division of Nanomedicine, Department of Medicine, California NanoSystems Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Spencer Melissa J.
(Molecular Biology Institute, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Spencer Melissa J.
(Center for Duchenne Muscular Dystrophy, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Spencer Melissa J.
(Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
,
Spencer Melissa J.
(Department of Neurology, University of California, Los Angeles, Los Angeles, CA, 90095, USA)
資料名:
Advanced Therapeutics
(Advanced Therapeutics)
巻:
2
号:
7
ページ:
e1900061
発行年:
2019年
JST資料番号:
W2672A
ISSN:
2366-3987
資料種別:
逐次刊行物 (A)
記事区分:
原著論文
発行国:
アメリカ合衆国 (USA)
言語:
英語 (EN)