文献
J-GLOBAL ID:202002276074865822
整理番号:20A0616873
すべてのジストロフィンのイソ型に影響を与える突然変異を有する2つのゲノム統合フリーDMD IPSC系統の生成とエクソンスキッピングに対する潜在的なamen性【JST・京大機械翻訳】
Generation of two genomic-integration-free DMD iPSC lines with mutations affecting all dystrophin isoforms and potentially amenable to exon-skipping
著者 (5件):
Ferrari Giulia
(Department of Cell and Developmental Biology, University College London, WC1E 6DE London, United Kingdom)
,
Muntoni Francesco
(Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, United Kingdom)
,
Muntoni Francesco
(NIHR Great Ormond Street Hospital Biomedical Research Centre, London, United Kingdom)
,
Tedesco Francesco Saverio
(Department of Cell and Developmental Biology, University College London, WC1E 6DE London, United Kingdom)
,
Tedesco Francesco Saverio
(Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, United Kingdom)
資料名:
Stem Cell Research (Web)
(Stem Cell Research (Web))
巻:
43
ページ:
Null
発行年:
2020年
JST資料番号:
U7041A
ISSN:
1873-5061
資料種別:
逐次刊行物 (A)
記事区分:
短報
発行国:
オランダ (NLD)
言語:
英語 (EN)