文献
J-GLOBAL ID:202102220587868728
整理番号:21A0080013
Fabry病におけるミガラスタット治療の長期有効性と安全性: 無作為化第3相ATTRACT研究のオープンラベル拡張による30か月の結果【JST・京大機械翻訳】
Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study
著者 (13件):
Feldt-Rasmussen Ulla
(Department of Medical Endocrinology and Metabolism, Rigshospitalet, Copenhagen University Hospital, Copenhagen, Denmark)
,
Hughes Derralynn
(Department of Haematology, Royal Free London NHS Foundation Trust and University College London, London, UK)
,
Sunder-Plassmann Gere
(Division of Nephrology and Dialysis, Department of Medicine III, Medical University of Vienna, Vienna, Austria)
,
Shankar Suma
(Department of Pediatrics, University of California-Davis, Davis, CA, USA)
,
Nedd Khan
(Infusion Associates, Grand Rapids, MI, USA)
,
Olivotto Iacopo
(Cardiomyopathy Unit, Careggi University Hospital, Florence, Italy)
,
Ortiz Damara
(Children’s Hospital of Pittsburgh, University of Pittsburgh Medical Center, Pittsburgh, PA, USA)
,
Ohashi Toya
(Jikei University Hospital, Tokyo, Japan)
,
Hamazaki Takashi
(Department of Pediatrics, Osaka City University Graduate School of Medicine, Osaka, Japan)
,
Skuban Nina
(Amicus Therapeutics, Inc., Cranbury, NJ, USA)
,
Yu Julie
(Amicus Therapeutics, Inc., Cranbury, NJ, USA)
,
Barth Jay A.
(Amicus Therapeutics, Inc., Cranbury, NJ, USA)
,
Nicholls Kathleen
(Department of Nephrology, Royal Melbourne Hospital, University of Melbourne, Parkville, VIC, Australia)
資料名:
Molecular Genetics and Metabolism
(Molecular Genetics and Metabolism)
巻:
131
号:
1-2
ページ:
219-228
発行年:
2020年
JST資料番号:
E0820A
ISSN:
1096-7192
資料種別:
逐次刊行物 (A)
記事区分:
原著論文
発行国:
オランダ (NLD)
言語:
英語 (EN)