文献
J-GLOBAL ID:202202214561613387
整理番号:22A0417613
神経変性疾患:混合骨格を持つ強力なアンチセンスオリゴヌクレオチドによる変異型C9orf72発現の抑制
Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide
著者 (22件):
TRAN Helene
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
YANG Huiya
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
MCKENNA-YASEK Diane
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
DOUTHWRIGHT Catherine L.
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
PINTO Courtney
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
METTERVILLE Jake
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
WEISS Alexandra
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
WIGHTMAN Nicholas
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
BROWN Robert H., Jr.
(Dep. of Neurology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
MOAZAMI Michael P.
(RNA Therapeutics Inst., Univ. Massachusetts Medical School, Worcester, MA, USA)
,
SHIN Minwook
(RNA Therapeutics Inst., Univ. Massachusetts Medical School, Worcester, MA, USA)
,
WATTS Jonathan K.
(RNA Therapeutics Inst., Univ. Massachusetts Medical School, Worcester, MA, USA)
,
SANIL Nitasha
(Res. Pharmacy, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
DOOLEY Craig
(Res. Pharmacy, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
PURI Ajit
(Dep. of Radiology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
GRAY-EDWARDS Heather
(Dep. of Radiology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
MAROSFOI Miklos
(Dep. of Radiology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
KING Robert M.
(Dep. of Radiology, Univ. Massachusetts Medical School, Worcester, MA, USA)
,
KING Robert M.
(Dep. of Biomedical Engineering, Worcester Polytechnic Inst., Worcester, MA, USA)
,
KENDERDINE Thomas
(Dep. of Chemistry, Univ. Connecticut, Storrs, CT, USA)
,
FABRIS Daniele
(Dep. of Chemistry, Univ. Connecticut, Storrs, CT, USA)
,
BOWSER Robert
(Departments of Neurology and Neurobiology, Barrow Neurological Inst., Phoenix, AZ, USA)
資料名:
Nature Medicine
(Nature Medicine)
巻:
28
号:
1
ページ:
117-124
発行年:
2022年01月
JST資料番号:
W0636A
ISSN:
1078-8956
資料種別:
逐次刊行物 (A)
記事区分:
原著論文
発行国:
アメリカ合衆国 (USA)
言語:
英語 (EN)