Art

J-GLOBAL ID：201902283089699792   Reference number：19A1345421

Special considerations for clinical trials in fibrodysplasia ossificans progressiva (FOP)

線維形成性骨化症(FOP)における臨床試験に関する特別な考察【JST・京大機械翻訳】

Author (22)： Hsiao Edward C. (Division of Endocrinology and Metabolism, and the Institute for Human Genetics, Department of Medicine, University of California, San Francisco, CA, USA) ,  Di Rocco Maja (Unit of Rare Diseases, Department of Pediatrics, IRCCS Giannina Gaslini Institute, Genoa, Italy) ,  Cali Amanda (Radiant Hope Foundation and the Ian Cali FOP Research Fund, PENN Medicine, Center for Research in FOP & Related Disorders) ,  Zasloff Michael (Departments of Orthopaedic Surgery and Genetics, The Center for Research in FOP & Related Disorders, University of Pennsylvania School of Medicine; and MedStar Georgetown Transplant Institute Georgetown University School of Medicine, Washington, DC, USA) ,  Al Mukaddam Mona (Division of Endocrinology, Diabetes and Metabolism, Departments of Medicine and Orthopaedic Surgery, University of Pennsylvania School of Medicine, Philadelphia, PA, USA) ,  Pignolo Robert J. (Department of Medicine, Mayo Clinic, Rochester, MN, USA) ,  Grunwald Zvi (Department of Anesthesiology, Thomas Jefferson University, Philadelphia, PA, USA) ,  Netelenbos Coen (Department of Internal Medicine section Endocrinology, Amsterdam Bone Center, Amsterdam University Medical Centers location VUmc, Amsterdam, the Netherlands) ,  Keen Richard (Royal National Orthopaedic Hospital, Stanmore, UK) ,  Baujat Genevieve (Centre de Reference Maladies Osseuses Constitutionnelles, Departement de Genetique, Hopital Necker-Enfants Malades, Institut Imagine, Paris, France) ,  Brown Matthew A. (Institute of Health and Biomedical Innovation, Queensland University of Technology, Translational Research Institute, Woolloongabba, QLD, Australia) ,  Cho Tae-Joon (Division of Pediatric Orthopaedics, Seoul National University Children’s Hospital, Seoul, South Korea) ,  De Cunto Carmen (Pediatric Rheumatology Section, Department of Pediatrics, Hospital Italiano de Buenos Aires, Ciudad Autonoma de Buenos Aires, Argentina) ,  Delai Patricia (Hospital Israelita Albert Einstein, Instituto de Ensino e Pesquisa, Sao Paulo-SP, Brazil) ,  Haga Nobuhiko (Department of Rehabilitation Medicine, Graduate School of Medicine, University of Tokyo, Tokyo, Japan) ,  Morhart Rolf (Department of Pediatrics, Klinikum Garmisch-Partenkirchen GmbH, Garmisch-Partenkirchen, Germany) ,  Scott Christiaan (Paediatric Rheumatology, Red Cross Children’s Hospital, University of Cape Town, Cape Town, South Africa) ,  Zhang Keqin (Department of Endocrinology, Tongji Hospital, Shanghai Tongji University, Shanghai, China) ,  Diecidue Robert J. (Sidney Kimmel Medical College, Thomas Jefferson University, Philadelphia, PA, USA) ,  Friedman Clive S. (Schulich School of Medicine and Dentistry, Pediatric Oral Health and Dentistry, London, ON, Canada) ,  Kaplan Fredrick S. (Departments of Medicine & Orthopaedic Surgery, Center for Research in FOP & Related Disorders, The Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA) ,  Eekhoff Elisabeth M.W. (Department of Internal Medicine section Endocrinology, Amsterdam Bone Center, Amsterdam University Medical Centers location VUmc, Amsterdam, the Netherlands)
Material： British Journal of Clinical Pharmacology  (BJCP)
Volume： 85  Issue： 6  Page： 1199-1207  Publication year： 2019 
JST Material Number： C0957B  ISSN： 0306-5251  Document type： Article
Article type： 文献レビュー  Country of issue： United States (USA)  Language： ENGLISH (EN)

Abstract/Point： Clinical trials for orphan dis...

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Thesaurus term： *clinical trial ,  human ,  *fibrous disease ,  Safety ,  robustness ,  blower ,  heterotopic ossification ,  Research Subjects
Semi thesaurus term： 臨床研究 ,  臨床ケア ,  *骨化症 , 【Automatic Indexing@JST】

Author keywords (3)： Fibrodysplasia ossificans progressiva (FOP) ,  patient safety ,  rare disease clinical trials

JST classification (1)： Clinical application of psychotropic drugs  (GW03110J)

Terms in the title (3)： 線維形成 ,  骨化症 ,  臨床試験