The University of Tokyo Center for Gene and Cell Therapy, The Institute of Medical Science
筋病学, 分子生物学, 腫瘍学, 脳神経外科学, 遺伝子治療, Molecular Biology, Oncology, Neurosurgery, Gene Therapy
Kazuhisa Takahashi, Tsutomu Igarashi, Koichi Miyake, Maika Kobayashi, Chiemi Yaguchi, Osamu Iijima, Yoshiyuki Yamazaki, Noriko Miyake, Shuhei Kameya, Takashi Shimada, et al. Efficient Transduction of Inner Retina by Surgical Internal Limiting Membrane (ILM) Peeling Before Intravitreal AAV Vector Injection in Cynomolgus Monkeys. MOLECULAR THERAPY. 2017. 25. 5. 111-111
Noriko Miyake, Koichi Miyake, Motoko Yamamoto, Takashi Shimada, Takashi Okada. Why Are scAAV9 Vectors Able to Pass Through the BBB but Not ssAAV9?; The Difference Between the ssAAV9 and scAAV9 Vector in Transduction of CNS by Intravenous Injection. MOLECULAR THERAPY. 2017. 25. 5. 320-321
M. Kobayashi, T. Igarashi, K. Miyake, N. Miyake, K. Nakamoto, Y. Hirai, H. Takahashi, T. Okada. Tyrosine-mutated AAV2 (Y730, 500, 444F) mediated BDNF rescued inner retina in rat retinal ischemic injury model. HUMAN GENE THERAPY. 2016. 27. 11. A122-A123
I. Omori, H. Yamaguchi, T. Kitano, N. Miyake, K. Miyake, D. Kazuo, K. Inokuchi. THE D816V C-KIT MUTATION HAS HIGHER ABILITY OF JAK-STAT AND SRC FAMILY KINASE THAN N822K C-KIT MUTATION, AND THEREFORE PROLIFERATION ACTIVITY IS HIGH IN CORE-BINDING FACTOR ACUTE MYELOID LEUKEMIA. HAEMATOLOGICA. 2015. 100. 353-354
Aki Nakamura, Koichi Miyake, Atsushi Watanabe, Yukihiko Hirai, Noriko Miyake, Osamu Iijima, Kumi Adachi, Hideaki Kinoshita, Taku Noguchi, Shinichi Abe, et al. Prolonged Survival and Improved Phenotypes of Lethal Hypophosphatasia Model Mice By Adeno-Associated Virus-Mediated Muscle Transduction of Bone-Targeted Alkaline Phosphatase. MOLECULAR THERAPY. 2015. 23. S282-S282
Ikuko Omori, Hiroki Yamaguchi, Tomoaki Kitano, Noriko Miyake, Koichi Miyake, Koiti Inokuchi. The D816V C-Kit Mutation Confers Higher Proliferation Activity By JAK-STAT and Src Family Kinase Pathways Compared to N822K C-Kit Mutation in Core-Binding Factor Acute Myeloid Leukemia. BLOOD. 2014. 124. 21
Noriko Miyake, Koichi Miyake, Atsushi Sakai, Motoko Yamamoto, Ayumi Endo, Hidenori Suzuki, Takashi Shimada. Gene Therapy for MLD by Intrathecal Administration of Type 9 AAV Vector Expressing ASA. JOURNAL OF GENE MEDICINE. 2014. 16. 7-8. 252-253
Koichi Miyake, Tae Matsumoto, Noriko Miyake, Hideo Orimo, Yoshitaka Fukunaga, Takashi Shimada. AAV Type 8 Mediated Bone-Targeted and Muscle Directed Neonatal Gene Therapy for Hypophosphatasia. JOURNAL OF GENE MEDICINE. 2014. 16. 7-8. 274-275
Nagisa Asakawa, Tsutomu Igarashi, Noriko Miyake, Koichi Miyake, Takashi Shimada, Hiroshi Takahashi. Direct Comparison of Administration Routes for AAV 8 Mediated Ocular Gene Therapy. JOURNAL OF GENE MEDICINE. 2014. 16. 7-8. 254-255
Tsutomu Igarashi, Koichi Miyake, Maika Kobayashi, Kazuhisa Takahashi, Noriko Miyake, Osamu Iijima, Kenji Nakamoto, Yukihiko Hirai, Takashi Shimada, Hiroshi Takahashi. Efficient Protection of Retina By Tyrosine-Mutated Self-Complementary AAV2 Vector Encoding BDNF in a Rat Retinal Ischemic Injury Model. MOLECULAR THERAPY. 2014. 22. S47-S47
Noriko Miyake, Koichi Miyake, Motoko Yamamoto, Takashi Shimada. Successful Treatment of Adult MLD Model Mice By Intravenous Injection of Self-Complementary Type 9 AAV Vector Expressing ASA. MOLECULAR THERAPY. 2014. 22. S151-S151
Noriko Miyake, Koichi Miyake, Takashi Shimada. Gene therapy of MLD model mice by intrathecal and intravenous injection of AAV9 vector. MOLECULAR GENETICS AND METABOLISM. 2014. 111. 2. S78-S79